After 5 years on oral treatment Evrysdi, 90% of children with SMA type 1 were alive, and many reached motor milestones, a ...

Muscle ultrasound helps assess muscle health and its association with motor function in SMA children treated with Spinraza, a ...

The latest understandings in SMA disease type, severity, and progression. Plus, how to make an accurate diagnosis and ...

The one-time gene therapy Itvisma will now be available for people with SMA of all ages in the European Union after winning ...

Columnist Brianna Albers says that moving out of her long-time home with SMA has turned out to be her biggest gamble yet.

I don’t talk to my ex anymore. For the sake of this column, I will have to let her know about it as a courtesy. But as far as a daily choice goes, it’s not one I make anymore. Readers who’ve kept up ...

My caregiver held the toothpaste tube in both hands, meticulously squishing it flat from the bottom all the way up to the nozzle. I laughed: “It’s OK, I have a whole new tube ready to go in the closet ...

SMA specialists face high rates of burnout and procrastination, delaying patient care. Burnout is linked to procrastination and reduced openness to innovative SMA treatments. Interventions addressing ...

Ice cream wasn’t always one of my favorite treats. Don’t get me wrong, I loved it, but it wasn’t one of my go-tos when I wanted something cold or sweet. I think SMA is part of what changed that. When ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google Parents of children with SMA reported significant unmet needs, ...

It’s been almost four months since my husband, Randy, and I made a hasty run to Charleston, South Carolina. Our mission was to adopt a dog our daughter, Katie, had found at a nearby rescue. This ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google Evrysdi (risdiplam) generally stabilized motor and respiratory ...