Thanks to in-utero blood transfusion technology, what was once a fatal diagnosis in the womb can now result in live births. However, this medical advancement created a new challenge: a growing ...
A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated ...
New research found that gene therapy for children with "bubble boy disease," or SCID, was successful in 95% of trial ...
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
The trial was small — just 12 children were treated in one or both ears — but it offers important lessons for researchers ...
An experimental genetic therapy can cure most cases of the 'Bubble Boy' disease, ADA-SCID. In the rare disorder, children are ...
Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed. A one-time gene therapy can markedly slow the progression of Huntington’s ...
A few months after launching its lead gene therapy into the clinic, Arbor Biotechnologies has found a European partner to come along for the ride. Italian pharma Chiesi is fertilizing Arbor’s rare ...
The move aims to regulate cell and gene therapies, and xenografts or animal-to-human transplants. Such therapies are ...
Shares of Krystal Biotech KRYS gained 3.9% yesterday after the company announced that it had dosed the first patient in a phase I/II study evaluating its eye drop KB801 for the treatment of ...
WILMINGTON, Mass.--(BUSINESS WIRE)--Charles River Laboratories International, Inc. (NYSE: CRL) and Elly’s Team, a parent-led foundation striving to find a cure for Neurodevelopmental Disorder with ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback